Gene Therapy Field Advances With Important Clinical Findings Reported in the New England Journal of Medicine
February 03 2009 - 9:00AM
PR Newswire (US)
SAN DIEGO, Calif., Feb. 3 /PRNewswire-FirstCall/ -- Cardium
Therapeutics (NYSE:CXM) today reported on recent clinical findings
published in The New England Journal of Medicine showing the
long-term outcome of a method of gene therapy to treat infant
children with a fatal disorder of the immune system. The infant
children studied had a rare form of severe combined
immunodeficiency (SCID). SCID arises in infants with a genetic
defect that leaves them unable to produce an enzyme called
adenosine deaminase. This key enzyme is most active in lymphocytes,
which are white blood cells vitally important for protection
against infection by bacteria, viruses and fungi. Infants who
inherit this fatal genetic abnormality develop impaired immune
responses, leading to recurrent infections and a failure to thrive.
Without adequate treatment, these children typically die within one
year of birth. (Logo:
http://www.newscom.com/cgi-bin/prnh/20051018/CARDIUMLOGO) The New
England Journal of Medicine (NEJM) reported on the success of a
DNA-based approach for the introduction of a normal adenosine
deaminase gene into the patient's hematopoietic stem cells that
have been removed from the bone marrow. After transfection of the
cells with the gene, the cells are re-infused back into the
patients after nonmyeloablative conditioning with busulfan. After a
single treatment, all 10 children in the study survived and gene
therapy was not associated with any adverse events during a median
follow-up of 4 years. In 8 of the 10 patients, there was excellent
and persistent immune reconstitution and protection from infection.
In an accompanying NEJM editorial entitled, Gene Therapy Fulfilling
Its Promise, the authors noted, "The prospects of continuing
advancement of gene therapy to wider applications remain strong.
Ongoing and upcoming clinical trials will use safer designs of
retroviral vectors, newer types of vectors for viral gene therapy,
and emerging methods for direct in situ gene repair. These
approaches to the treatment of hemoglobinopathies, hemophilia,
muscular dystrophy, congenital retinopathies, neurodegenerative
disorders, and other genetic diseases may further fulfill the
promise that gene therapy made two decades ago." "Historically,
gene therapy has been long on promises and, all too often, short on
clinical results. The success of this recent study marks an
important milestone for the field, provides important insights into
the use of advanced gene therapies, and sheds new light on the
promise and new therapeutic realties of DNA-based approaches for
the treatment of disease," stated Christopher J. Reinhard, Chairman
and Chief Executive Officer of Cardium Therapeutics. "Cardium is
developing a new class of growth factor biologics designed to take
advantage of the body's own natural healing abilities for the
regenerative treatment of ischemic conditions, such as chronic
wounds, myocardial ischemia and heart attacks, and we look forward
to completing our Phase 2b MATRIX gene therapy clinical trial that
is evaluating the safety and efficacy of Excellarate for the
potential treatment of non-healing diabetic foot ulcers." About
Cardium Cardium Therapeutics, Inc. and its subsidiaries, InnerCool
Therapies, Inc. and the Tissue Repair Company, are medical
technology companies primarily focused on the development,
manufacture and sale of innovative therapeutic products and devices
for cardiovascular, ischemic and related indications. Cardium's
InnerCool Therapies subsidiary is a San Diego-based medical
technology company in the emerging field of temperature modulation
therapy to rapidly and controllably cool the body in order to
reduce cell death and damage following acute ischemic events such
as cardiac arrest or stroke, and to potentially lessen or prevent
associated injuries such as adverse neurological outcomes. For more
information about Cardium's InnerCool subsidiary and patient
temperature modulation, including InnerCool's new RapidBlue(TM)
System, which just received FDA clearance, and its CoolBlue(TM)
System, please visit http://www.innercool.com/. Cardium also has
two biologic candidates in clinical development. Cardium's Tissue
Repair Company subsidiary (TRC) is focused on the development of
growth factor therapeutics for the treatment of severe chronic
diabetic wounds. TRC's lead product candidate, Excellarate(TM), is
a DNA-activated collagen gel for topical treatment formulated with
an adenovector delivery carrier encoding human platelet-derived
growth factor-BB (PDGF-BB). Excellarate(TM) is initially being
developed to be administered once or twice for the potential
treatment of non-healing diabetic foot ulcers. Other potential
applications for TRC's Gene Activated Matrix(TM) (GAM) technology
include therapeutic angiogenesis (cardiovascular ischemia,
peripheral arterial disease) and orthopedic products, including
hard tissue (bone) and soft tissue (ligament, tendon, cartilage)
repair. For more information about Cardium's Tissue Repair Company
subsidiary, please visit http://www.t-r-co.com/. Cardium's Generx
product candidate (alferminogene tadenovec, Ad5FGF-4) is a
DNA-based growth factor therapeutic being developed for potential
use by interventional cardiologists as a one-time treatment to
promote and stimulate the growth of collateral circulation in the
hearts of patients with ischemic conditions such as recurrent
angina. For more information about Cardium Therapeutics and its
businesses, products and therapeutic candidates, please visit
http://www.cardiumthx.com/ or view its most recent Annual Report at
http://www.cardiumthx.com/flash/pdf/CardiumAR07_Book_FINAL.pdf.
Forward-Looking Statements Except for statements of historical
fact, the matters discussed in this press release are forward
looking and reflect numerous assumptions and involve a variety of
risks and uncertainties, many of which are beyond our control and
may cause actual results to differ materially from stated
expectations. For example, there can be no assurance that results
or trends observed in one clinical study or procedure will be
reproduced in subsequent studies or procedures, that human clinical
trials can be conducted and completed in an efficient and
successful manner, that FDA, CE Mark or other regulatory clearances
or UL or other certifications, or partnering or other distribution
agreements or other commercialization efforts will be successful or
will effectively accelerate the business or market, that product
modifications or launches will be successful or that the resulting
products will be favorably received in the marketplace, that our
products or product candidates will prove to be sufficiently safe
and effective, that necessary regulatory approvals will be
obtained, that third parties on whom we depend will perform as
anticipated, or that our products or product candidates will not be
unfavorably compared to competitive products that may be regarded
as safer, more effective, easier to use or less expensive. Actual
results may also differ substantially from those described in or
contemplated by this press release due to risks and uncertainties
that exist in our operations and business environment, including,
without limitation, risks and uncertainties that are inherent in
the development of complex biologics and therapeutic hypothermia
devices and in the conduct of human clinical trials, including the
timing, costs and outcomes of such trials, our ability to obtain
necessary funding, regulatory approvals and expected
qualifications, our ability to successfully accelerate the
commercialization of our therapeutic hypothermia devices and launch
new devices within the timeframes contemplated, our dependence upon
proprietary technology, our history of operating losses and
accumulated deficits, our reliance on collaborative relationships
and critical personnel, and current and future competition, as well
as other risks described from time to time in filings we make with
the Securities and Exchange Commission. We undertake no obligation
to release publicly the results of any revisions to these
forward-looking statements to reflect events or circumstances
arising after the date hereof. Copyright 2009 Cardium Therapeutics,
Inc. All rights reserved. For Terms of Use Privacy Policy, please
visit http://www.cardiumthx.com/. Cardium Therapeutics(TM) and
Generx(TM) are trademarks of Cardium Therapeutics, Inc. Tissue
Repair(TM), Gene Activated Matrix(TM), GAM(TM) and Excellarate(TM)
are trademarks of Tissue Repair Company. InnerCool Therapies(R),
InnerCool(R), Celsius Control System(R), RapidBlue(TM),
CoolBlue(TM). Accutrol(R), Temperature Control Element(R) and
TCE(R) and UroCool(TM) are trademarks of InnerCool Therapies, Inc.
(other trademarks belong to their respective owners)
http://www.newscom.com/cgi-bin/prnh/20051018/CARDIUMLOGO
http://photoarchive.ap.org/ DATASOURCE: Cardium Therapeutics
CONTACT: Bonnie Ortega, Director, Investor/Public Relations of
Cardium Therapeutics, Inc., +1-858-436-1018, Web site:
http://www.cardiumthx.com/ http://www.t-r-co.com/
http://www.innercool.com/
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