georgie18
2 days ago
SGMO...$2.53...Fins after close...🥳
georgie18
Member Level
Re: georgie18 post# 664188
Friday, November 08, 2024 11:09:45 AM
Post#
664225
of 664553
SGMO...$3.10s clearing here...🥳
georgie18
Member Level
Re: georgie18 post# 385366
Friday, November 08, 2024 9:21:06 AM
Post#
385382
of 385395
SGMO...$3...🥳...Been waiting for this ..."W" in play here...$6 target for me...
georgie18
Member Level
Re: georgie18 post# 663989
Thursday, November 07, 2024 2:23:36 PM
Post#
664113
of 664186
SGMO...$2.83...🥳
georgie18
Member Level
Re: georgie18 post# 385311
Thursday, November 07, 2024 9:59:59 AM
Post#
385341
of 385365
SGMO...$2.65s clearing here...This was as low as .30 in July...🥳
georgie18
Member Level
Re: georgie18 post# 663756
Wednesday, November 06, 2024 2:50:09 PM
Post#
663878
of 663987
SGMO...$2.45...HOD..."W" Pattern in play here...Target $6...🥳https://schrts.co/dEUXVUBf
SGMO...$2.25...🥳
georgie18
Member Level
Re: georgie18 post# 663703
Tuesday, November 05, 2024 3:35:51 PM
Post#
663735
of 663755
SGMO...$2.14...HOD...🥳
georgie18
Member Level
Re: georgie18 post# 663630
Tuesday, November 05, 2024 1:25:37 PM
Post#
663703
of 663733
SGMO...$2.02...🥳...On Tuesday, H.C. Wainwright adjusted its outlook on shares of Sangamo BioSciences (NASDAQ:SGMO), raising the price target to $10 from the previous $5, while maintaining a Buy rating on the company's stock. The revision follows Sangamo's announcement on October 22, 2024, regarding a productive Type B meeting with the FDA about its gene therapy program for Fabry disease, isaralgagene civaparvovec (ST-920 or isa-vec).
The FDA has acknowledged that data from the ongoing Phase 1/2 STAAR trial could serve as the primary evidence for an accelerated approval process. This development could lead to a faster and more cost-effective path to submitting a Biologics License Application (BLA) than initially anticipated.
Member Level
Re: georgie18 post# 663012
Monday, November 04, 2024 4:27:39 PM
Post#
663630
of 663703
SGMO...$1.77...Fins will be announced after close on Nov 12,2024...🥳
- U.S. Food and Drug Administration (FDA) provides a clear regulatory pathway to Accelerated Approval for isaralgagene civaparvovec using data from ongoing Phase 1/2 STAAR study, avoiding requirement for additional registrational study and accelerating estimated time to potential approval by approximately three years.
- FDA confirms that estimated glomerular filtration rate (eGFR) slope data at one year across all Phase 1/2 patients can serve as primary basis for approval under Accelerated Approval pathway.
- Data to support Accelerated Approval pathway available in first half of 2025, with a potential Biologics License Application (BLA) submission expected in the second half of 2025.
georgie18
6 days ago
SGMO...$3.10s clearing here...🥳
georgie18
Member Level
Re: georgie18 post# 385366
Friday, November 08, 2024 9:21:06 AM
Post#
385382
of 385395
SGMO...$3...🥳...Been waiting for this ..."W" in play here...$6 target for me...
georgie18
Member Level
Re: georgie18 post# 663989
Thursday, November 07, 2024 2:23:36 PM
Post#
664113
of 664186
SGMO...$2.83...🥳
georgie18
Member Level
Re: georgie18 post# 385311
Thursday, November 07, 2024 9:59:59 AM
Post#
385341
of 385365
SGMO...$2.65s clearing here...This was as low as .30 in July...🥳
georgie18
Member Level
Re: georgie18 post# 663756
Wednesday, November 06, 2024 2:50:09 PM
Post#
663878
of 663987
SGMO...$2.45...HOD..."W" Pattern in play here...Target $6...🥳https://schrts.co/dEUXVUBf
SGMO...$2.25...🥳
georgie18
Member Level
Re: georgie18 post# 663703
Tuesday, November 05, 2024 3:35:51 PM
Post#
663735
of 663755
SGMO...$2.14...HOD...🥳
georgie18
Member Level
Re: georgie18 post# 663630
Tuesday, November 05, 2024 1:25:37 PM
Post#
663703
of 663733
SGMO...$2.02...🥳...On Tuesday, H.C. Wainwright adjusted its outlook on shares of Sangamo BioSciences (NASDAQ:SGMO), raising the price target to $10 from the previous $5, while maintaining a Buy rating on the company's stock. The revision follows Sangamo's announcement on October 22, 2024, regarding a productive Type B meeting with the FDA about its gene therapy program for Fabry disease, isaralgagene civaparvovec (ST-920 or isa-vec).
The FDA has acknowledged that data from the ongoing Phase 1/2 STAAR trial could serve as the primary evidence for an accelerated approval process. This development could lead to a faster and more cost-effective path to submitting a Biologics License Application (BLA) than initially anticipated.
Member Level
Re: georgie18 post# 663012
Monday, November 04, 2024 4:27:39 PM
Post#
663630
of 663703
SGMO...$1.77...Fins will be announced after close on Nov 12,2024...🥳
- U.S. Food and Drug Administration (FDA) provides a clear regulatory pathway to Accelerated Approval for isaralgagene civaparvovec using data from ongoing Phase 1/2 STAAR study, avoiding requirement for additional registrational study and accelerating estimated time to potential approval by approximately three years.
- FDA confirms that estimated glomerular filtration rate (eGFR) slope data at one year across all Phase 1/2 patients can serve as primary basis for approval under Accelerated Approval pathway.
- Data to support Accelerated Approval pathway available in first half of 2025, with a potential Biologics License Application (BLA) submission expected in the second half of 2025.
georgie18
6 days ago
SGMO...$3...🥳...Been waiting for this ..."W" in play here...$6 target for me...
georgie18
Member Level
Re: georgie18 post# 663989
Thursday, November 07, 2024 2:23:36 PM
Post#
664113
of 664186
SGMO...$2.83...🥳
georgie18
Member Level
Re: georgie18 post# 385311
Thursday, November 07, 2024 9:59:59 AM
Post#
385341
of 385365
SGMO...$2.65s clearing here...This was as low as .30 in July...🥳
georgie18
Member Level
Re: georgie18 post# 663756
Wednesday, November 06, 2024 2:50:09 PM
Post#
663878
of 663987
SGMO...$2.45...HOD..."W" Pattern in play here...Target $6...🥳https://schrts.co/dEUXVUBf
SGMO...$2.25...🥳
georgie18
Member Level
Re: georgie18 post# 663703
Tuesday, November 05, 2024 3:35:51 PM
Post#
663735
of 663755
SGMO...$2.14...HOD...🥳
georgie18
Member Level
Re: georgie18 post# 663630
Tuesday, November 05, 2024 1:25:37 PM
Post#
663703
of 663733
SGMO...$2.02...🥳...On Tuesday, H.C. Wainwright adjusted its outlook on shares of Sangamo BioSciences (NASDAQ:SGMO), raising the price target to $10 from the previous $5, while maintaining a Buy rating on the company's stock. The revision follows Sangamo's announcement on October 22, 2024, regarding a productive Type B meeting with the FDA about its gene therapy program for Fabry disease, isaralgagene civaparvovec (ST-920 or isa-vec).
The FDA has acknowledged that data from the ongoing Phase 1/2 STAAR trial could serve as the primary evidence for an accelerated approval process. This development could lead to a faster and more cost-effective path to submitting a Biologics License Application (BLA) than initially anticipated.
Member Level
Re: georgie18 post# 663012
Monday, November 04, 2024 4:27:39 PM
Post#
663630
of 663703
SGMO...$1.77...Fins will be announced after close on Nov 12,2024...🥳
- U.S. Food and Drug Administration (FDA) provides a clear regulatory pathway to Accelerated Approval for isaralgagene civaparvovec using data from ongoing Phase 1/2 STAAR study, avoiding requirement for additional registrational study and accelerating estimated time to potential approval by approximately three years.
- FDA confirms that estimated glomerular filtration rate (eGFR) slope data at one year across all Phase 1/2 patients can serve as primary basis for approval under Accelerated Approval pathway.
- Data to support Accelerated Approval pathway available in first half of 2025, with a potential Biologics License Application (BLA) submission expected in the second half of 2025.
georgie18
7 days ago
SGMO...$2.83...🥳
georgie18
Member Level
Re: georgie18 post# 385311
Thursday, November 07, 2024 9:59:59 AM
Post#
385341
of 385365
SGMO...$2.65s clearing here...This was as low as .30 in July...🥳
georgie18
Member Level
Re: georgie18 post# 663756
Wednesday, November 06, 2024 2:50:09 PM
Post#
663878
of 663987
SGMO...$2.45...HOD..."W" Pattern in play here...Target $6...🥳https://schrts.co/dEUXVUBf
SGMO...$2.25...🥳
georgie18
Member Level
Re: georgie18 post# 663703
Tuesday, November 05, 2024 3:35:51 PM
Post#
663735
of 663755
SGMO...$2.14...HOD...🥳
georgie18
Member Level
Re: georgie18 post# 663630
Tuesday, November 05, 2024 1:25:37 PM
Post#
663703
of 663733
SGMO...$2.02...🥳...On Tuesday, H.C. Wainwright adjusted its outlook on shares of Sangamo BioSciences (NASDAQ:SGMO), raising the price target to $10 from the previous $5, while maintaining a Buy rating on the company's stock. The revision follows Sangamo's announcement on October 22, 2024, regarding a productive Type B meeting with the FDA about its gene therapy program for Fabry disease, isaralgagene civaparvovec (ST-920 or isa-vec).
The FDA has acknowledged that data from the ongoing Phase 1/2 STAAR trial could serve as the primary evidence for an accelerated approval process. This development could lead to a faster and more cost-effective path to submitting a Biologics License Application (BLA) than initially anticipated.
Member Level
Re: georgie18 post# 663012
Monday, November 04, 2024 4:27:39 PM
Post#
663630
of 663703
SGMO...$1.77...Fins will be announced after close on Nov 12,2024...🥳
- U.S. Food and Drug Administration (FDA) provides a clear regulatory pathway to Accelerated Approval for isaralgagene civaparvovec using data from ongoing Phase 1/2 STAAR study, avoiding requirement for additional registrational study and accelerating estimated time to potential approval by approximately three years.
- FDA confirms that estimated glomerular filtration rate (eGFR) slope data at one year across all Phase 1/2 patients can serve as primary basis for approval under Accelerated Approval pathway.
- Data to support Accelerated Approval pathway available in first half of 2025, with a potential Biologics License Application (BLA) submission expected in the second half of 2025.
georgie18
7 days ago
SGMO...$2.65s clearing here...This was as low as .30 in July...🥳
georgie18
Member Level
Re: georgie18 post# 663756
Wednesday, November 06, 2024 2:50:09 PM
Post#
663878
of 663987
SGMO...$2.45...HOD..."W" Pattern in play here...Target $6...🥳https://schrts.co/dEUXVUBf
SGMO...$2.25...🥳
georgie18
Member Level
Re: georgie18 post# 663703
Tuesday, November 05, 2024 3:35:51 PM
Post#
663735
of 663755
SGMO...$2.14...HOD...🥳
georgie18
Member Level
Re: georgie18 post# 663630
Tuesday, November 05, 2024 1:25:37 PM
Post#
663703
of 663733
SGMO...$2.02...🥳...On Tuesday, H.C. Wainwright adjusted its outlook on shares of Sangamo BioSciences (NASDAQ:SGMO), raising the price target to $10 from the previous $5, while maintaining a Buy rating on the company's stock. The revision follows Sangamo's announcement on October 22, 2024, regarding a productive Type B meeting with the FDA about its gene therapy program for Fabry disease, isaralgagene civaparvovec (ST-920 or isa-vec).
The FDA has acknowledged that data from the ongoing Phase 1/2 STAAR trial could serve as the primary evidence for an accelerated approval process. This development could lead to a faster and more cost-effective path to submitting a Biologics License Application (BLA) than initially anticipated.
Member Level
Re: georgie18 post# 663012
Monday, November 04, 2024 4:27:39 PM
Post#
663630
of 663703
SGMO...$1.77...Fins will be announced after close on Nov 12,2024...🥳
- U.S. Food and Drug Administration (FDA) provides a clear regulatory pathway to Accelerated Approval for isaralgagene civaparvovec using data from ongoing Phase 1/2 STAAR study, avoiding requirement for additional registrational study and accelerating estimated time to potential approval by approximately three years.
- FDA confirms that estimated glomerular filtration rate (eGFR) slope data at one year across all Phase 1/2 patients can serve as primary basis for approval under Accelerated Approval pathway.
- Data to support Accelerated Approval pathway available in first half of 2025, with a potential Biologics License Application (BLA) submission expected in the second half of 2025.
georgie18
1 week ago
SGMO...$2.45...HOD..."W" Pattern in play here...Target $6...🥳https://schrts.co/dEUXVUBf
SGMO...$2.25...🥳
georgie18
Member Level
Re: georgie18 post# 663703
Tuesday, November 05, 2024 3:35:51 PM
Post#
663735
of 663755
SGMO...$2.14...HOD...🥳
georgie18
Member Level
Re: georgie18 post# 663630
Tuesday, November 05, 2024 1:25:37 PM
Post#
663703
of 663733
SGMO...$2.02...🥳...On Tuesday, H.C. Wainwright adjusted its outlook on shares of Sangamo BioSciences (NASDAQ:SGMO), raising the price target to $10 from the previous $5, while maintaining a Buy rating on the company's stock. The revision follows Sangamo's announcement on October 22, 2024, regarding a productive Type B meeting with the FDA about its gene therapy program for Fabry disease, isaralgagene civaparvovec (ST-920 or isa-vec).
The FDA has acknowledged that data from the ongoing Phase 1/2 STAAR trial could serve as the primary evidence for an accelerated approval process. This development could lead to a faster and more cost-effective path to submitting a Biologics License Application (BLA) than initially anticipated.
Member Level
Re: georgie18 post# 663012
Monday, November 04, 2024 4:27:39 PM
Post#
663630
of 663703
SGMO...$1.77...Fins will be announced after close on Nov 12,2024...🥳
- U.S. Food and Drug Administration (FDA) provides a clear regulatory pathway to Accelerated Approval for isaralgagene civaparvovec using data from ongoing Phase 1/2 STAAR study, avoiding requirement for additional registrational study and accelerating estimated time to potential approval by approximately three years.
- FDA confirms that estimated glomerular filtration rate (eGFR) slope data at one year across all Phase 1/2 patients can serve as primary basis for approval under Accelerated Approval pathway.
- Data to support Accelerated Approval pathway available in first half of 2025, with a potential Biologics License Application (BLA) submission expected in the second half of 2025.
georgie18
1 week ago
SGMO...$2.25...🥳
georgie18
Member Level
Re: georgie18 post# 663703
Tuesday, November 05, 2024 3:35:51 PM
Post#
663735
of 663755
SGMO...$2.14...HOD...🥳
georgie18
Member Level
Re: georgie18 post# 663630
Tuesday, November 05, 2024 1:25:37 PM
Post#
663703
of 663733
SGMO...$2.02...🥳...On Tuesday, H.C. Wainwright adjusted its outlook on shares of Sangamo BioSciences (NASDAQ:SGMO), raising the price target to $10 from the previous $5, while maintaining a Buy rating on the company's stock. The revision follows Sangamo's announcement on October 22, 2024, regarding a productive Type B meeting with the FDA about its gene therapy program for Fabry disease, isaralgagene civaparvovec (ST-920 or isa-vec).
The FDA has acknowledged that data from the ongoing Phase 1/2 STAAR trial could serve as the primary evidence for an accelerated approval process. This development could lead to a faster and more cost-effective path to submitting a Biologics License Application (BLA) than initially anticipated.
Member Level
Re: georgie18 post# 663012
Monday, November 04, 2024 4:27:39 PM
Post#
663630
of 663703
SGMO...$1.77...Fins will be announced after close on Nov 12,2024...🥳
- U.S. Food and Drug Administration (FDA) provides a clear regulatory pathway to Accelerated Approval for isaralgagene civaparvovec using data from ongoing Phase 1/2 STAAR study, avoiding requirement for additional registrational study and accelerating estimated time to potential approval by approximately three years.
- FDA confirms that estimated glomerular filtration rate (eGFR) slope data at one year across all Phase 1/2 patients can serve as primary basis for approval under Accelerated Approval pathway.
- Data to support Accelerated Approval pathway available in first half of 2025, with a potential Biologics License Application (BLA) submission expected in the second half of 2025.
georgie18
1 week ago
SGMO...$2.14...HOD...🥳
georgie18
Member Level
Re: georgie18 post# 663630
Tuesday, November 05, 2024 1:25:37 PM
Post#
663703
of 663733
SGMO...$2.02...🥳...On Tuesday, H.C. Wainwright adjusted its outlook on shares of Sangamo BioSciences (NASDAQ:SGMO), raising the price target to $10 from the previous $5, while maintaining a Buy rating on the company's stock. The revision follows Sangamo's announcement on October 22, 2024, regarding a productive Type B meeting with the FDA about its gene therapy program for Fabry disease, isaralgagene civaparvovec (ST-920 or isa-vec).
The FDA has acknowledged that data from the ongoing Phase 1/2 STAAR trial could serve as the primary evidence for an accelerated approval process. This development could lead to a faster and more cost-effective path to submitting a Biologics License Application (BLA) than initially anticipated.
Member Level
Re: georgie18 post# 663012
Monday, November 04, 2024 4:27:39 PM
Post#
663630
of 663703
SGMO...$1.77...Fins will be announced after close on Nov 12,2024...🥳
- U.S. Food and Drug Administration (FDA) provides a clear regulatory pathway to Accelerated Approval for isaralgagene civaparvovec using data from ongoing Phase 1/2 STAAR study, avoiding requirement for additional registrational study and accelerating estimated time to potential approval by approximately three years.
- FDA confirms that estimated glomerular filtration rate (eGFR) slope data at one year across all Phase 1/2 patients can serve as primary basis for approval under Accelerated Approval pathway.
- Data to support Accelerated Approval pathway available in first half of 2025, with a potential Biologics License Application (BLA) submission expected in the second half of 2025.
georgie18
1 week ago
SGMO...$2.02...🥳...On Tuesday, H.C. Wainwright adjusted its outlook on shares of Sangamo BioSciences (NASDAQ:SGMO), raising the price target to $10 from the previous $5, while maintaining a Buy rating on the company's stock. The revision follows Sangamo's announcement on October 22, 2024, regarding a productive Type B meeting with the FDA about its gene therapy program for Fabry disease, isaralgagene civaparvovec (ST-920 or isa-vec).
The FDA has acknowledged that data from the ongoing Phase 1/2 STAAR trial could serve as the primary evidence for an accelerated approval process. This development could lead to a faster and more cost-effective path to submitting a Biologics License Application (BLA) than initially anticipated.
Member Level
Re: georgie18 post# 663012
Monday, November 04, 2024 4:27:39 PM
Post#
663630
of 663703
SGMO...$1.77...Fins will be announced after close on Nov 12,2024...🥳
- U.S. Food and Drug Administration (FDA) provides a clear regulatory pathway to Accelerated Approval for isaralgagene civaparvovec using data from ongoing Phase 1/2 STAAR study, avoiding requirement for additional registrational study and accelerating estimated time to potential approval by approximately three years.
- FDA confirms that estimated glomerular filtration rate (eGFR) slope data at one year across all Phase 1/2 patients can serve as primary basis for approval under Accelerated Approval pathway.
- Data to support Accelerated Approval pathway available in first half of 2025, with a potential Biologics License Application (BLA) submission expected in the second half of 2025.
INV4
2 weeks ago
Good morning and thank you jondoeuk. Many of these types of companies struggle at first, but when they have a 'hit', things can turn around quickly. We'll have to wait and see IMHO.
Unless they upgrade their tech to include additional tools
News Release:
Sangamo Therapeutics Announces Alignment With FDA on Accelerated Approval Pathway for ST-920 in Fabry Disease With BLA Submission Expected in 2025
October 22, 2024
- U.S. Food and Drug Administration (FDA) provides a clear regulatory pathway to Accelerated Approval for isaralgagene civaparvovec using data from ongoing Phase 1/2 STAAR study, avoiding requirement for additional registrational study and accelerating estimated time to potential approval by approximately three years.
- FDA confirms that estimated glomerular filtration rate (eGFR) slope data at one year across all Phase 1/2 patients can serve as primary basis for approval under Accelerated Approval pathway.
- Data to support Accelerated Approval pathway available in first half of 2025, with a potential Biologics License Application (BLA) submission expected in the second half of 2025.
RICHMOND, Calif.--(BUSINESS WIRE)--Oct. 22, 2024-- Sangamo Therapeutics, Inc. (Nasdaq: SGMO), a genomic medicine company, today announced the outcome of a recent successful interaction with the U.S. FDA, providing a clear regulatory pathway to Accelerated Approval for isaralgagene civaparvovec, or ST-920, its wholly owned gene therapy product candidate for the treatment of Fabry disease...
https://investor.sangamo.com/news-releases/news-release-details/sangamo-therapeutics-announces-alignment-fda-accelerated
$SGMO
jondoeuk
2 weeks ago
Pioneering the future of genomic medicine? The company was founded in 1995. Gene editing has evolved. Unless they upgrade their tech to include additional tools I can't seem them being a meaningful player in any way. Too many failures* in their long history. Another issue is the management.
* This includes diabetic neuropathy, HIV, IVPRP, TDT/SCD, oncology (with GILD), and CNS (with BIIB and NVS). Investments in CAR-Tregs (and elsewhere) were written off. Also, programs in Huntington's, ALS, and others that still have not gotten off the ground. They were touting base editing at one point. But not to worry, they pivoted again!
INV4
2 weeks ago
It's an older article, but good to read about $SGMO:
15 Biotech Stocks Wall Street Analysts Say Are Too Cheap
Of the stocks that topped our screen, prominent names include Sangamo Therapeutics
Sangamo Biosciences Inc (SGMO), which develops gene therapies and cell therapies, among other technologies. The company has a long of partnering with big pharma companies, including Pfizer.
Its stock is down 86% over the past three years, and traded recently at $1.16 (today / at the moment $1.87-ish). Analysts see significant opportunities for growth: The average target price among analysts is $7.38, implying a potential gain of more than 500%.
https://www.marketwatch.com/articles/15-biotech-stocks-wall-street-analysts-cheap-9da65e89?mod=mw_quote_news
$SGMO
INV4
2 weeks ago
Hemophilia A
Giroctocogene fitelparvovec
(formerly known as SB-525 or PF-07055480)
Status: Phase 3
Partner: partnered with Pfizer / transitioned to Pfizer for Phase 3 development
Technology: Liver-targeted AAV gene therapy
Disease
Hemophilia A is a rare bleeding disorder caused by mutations in the F8 gene, resulting in a deficiency of clotting factor VIII (FVIII), a protein that is required for normal blood clotting. The severity of hemophilia is determined by the amount of FVIII in the blood. The lower the amount of FVIII, the more likely it is that bleeding will occur, which can lead to serious health problems.
Hemophilia A occurs in approximately one in every 5,000-10,000 male births worldwide. For people who live with hemophilia A, there is an increased risk of spontaneous bleeding as well as bleeding following injuries or surgery. It is a lifelong disease that requires constant monitoring and therapy.
Genomic medicine approach
Giroctocogene fitelparvovec is a liver-tropic rAAV6 vector carrying a B-domain deleted F8 gene that is delivered through a single IV infusion. Giroctocogene fitelparvovec aims to deliver a working copy of the F8 gene to the liver so that liver cells can start producing functional FVIII clotting factor.
Phase 3 Study AFFINE
The Phase 3 AFFINE (NCT04370054) study is an open-label, single-dose, single-arm, multicenter study to evaluate the efficacy and safety of a single infusion of giroctocogene fitelparvovec in more than 60 adult (ages 18-64 years) male participants with moderately severe to severe hemophilia A. Eligible study participants will have completed at least six months of routine FVIII prophylaxis therapy during the lead-in Phase 3 study (NCT03587116) in order to collect pretreatment data for efficacy and selected safety parameters.
The primary endpoint is impact on annualized bleeding rate (ABR) through 12 months following treatment with giroctocogene fitelparvovec. This will be compared to ABR on prior FVIII prophylaxis replacement therapy. The secondary endpoints include FVIII activity level after the onset of steady state and through 12 months following infusion of giroctocogene fitelparvovec.
Clinical Trial Details: clinicaltrials.gov
https://www.sangamo.com/programs/clinical-trials/hemophilia-a/
$SGMO
INV4
2 weeks ago
Pioneering the future of genomic medicine
Sangamo uses its deep scientific expertise and proprietary zinc finger technology to create genomic cures for patients suffering from severe diseases for which todayβs medicine can only offer symptom management at best.
Sangamo is using groundbreaking science and novel technology to replace todayβs symptomatic treatments with tomorrowβs genomic cures.
PIPELINE:
- Chronic Neuropathic Pain (Nav 1.7)
- Prion Disease
- Tauopathies
- ALS/FTD
- Huntington's Disease
OTHER PROGRAMS:
- Hemophilia A (Giroctogene fitelparvovec)
Data presented at ASH 2023
July 2024: Positive topline readout in Phase 3 AFFINE trial. Pfizer plans to discuss data with regulatory authorities in coming months.
- Fabry Disease (Isaralgagene civaparvovec)
Data presented at WORLDSymposium 2024
Continue to amass encouraging clinical data. Potential partnership discussions ongoing.
https://www.sangamo.com/programs/#pipeline
=========
Sangamo Therapeutics, Inc. is a clinical stage biotechnology company, which engages in the research and development of zinc finger proteins. It focuses on three therapeutic areas: inherited metabolic diseases, central nervous system, and diseases and immunology, which consist of inflammatory and autoimmune diseases. It also offers complementary technology platforms such as gene therapy, ex vivo cell therapy, in vivo genome editing, and in vivo genome regulation. The company was founded by Edward O. Lanphier II in 1995 and is headquartered in Richmond, CA.
https://www.marketwatch.com/investing/stock/sgmo
$SGMO