farrell90
7 years ago
Spark Therapeutics achieves gene therapy breakthrough.The approval gives hope to patients suffering from genetic retinal diseases as well as other genetic disorders.
Spark's, Luxturna, approved by FDA for treatment of inherited retinal disorder RPE65 a cause of the genetic disorder also known as Leber's Congenital Amaurosis.
"The U.S. Food and Drug Administration today approved Luxturna (voretigene neparvovec-rzyl), a new gene therapy, to treat children and adult patients with an inherited form of vision loss that may result in blindness. Luxturna is the first directly administered gene therapy approved in the U.S. that targets a disease caused by mutations in a specific gene."
Todayβs approval marks another first in the field of gene therapy β both in how the therapy works and in expanding the use of gene therapy beyond the treatment of cancer to the treatment of vision loss β and this milestone reinforces the potential of this breakthrough approach in treating a wide-range of challenging diseases. The culmination of decades of research has resulted in three gene therapy approvals this year for patients with serious and rare diseases. I believe gene therapy will become a mainstay in treating, and maybe curing, many of our most devastating and intractable illnesses,β said FDA Commissioner Scott Gottlieb, M.D. βWeβre at a turning point when it comes to this novel form of therapy and at the FDA, weβre focused on establishing the right policy framework to capitalize on this scientific opening. Next year, weβll begin issuing a suite of disease-specific guidance documents on the development of specific gene therapy products to lay out modern and more efficient parameters β including new clinical measures β for the evaluation and review of gene therapy for different high-priority diseases where the platform is being targeted.β
Luxturna is approved for the treatment of patients with confirmed biallelic RPE65 mutation-associated retinal dystrophy that leads to vision loss and may cause complete blindness in certain patients.
https://www.fda.gov/NewsEvents/Newsroom/PressAnnouncements/ucm589467.htm
Good luck, Farrell
stocktrademan
10 years ago
$ONCE recent news/filings
bullish
## source: finance.yahoo.com
Tue, 19 May 2015 17:04:26 GMT ~ SPARK THERAPEUTICS, INC. Financials
read full: http://finance.yahoo.com/q/is?s=once
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Mon, 11 May 2015 20:45:05 GMT ~ SPARK THERAPEUTICS, INC. Files SEC form 10-Q, Quarterly Report
read full: http://biz.yahoo.com/e/150511/once10-q.html
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Wed, 06 May 2015 12:30:00 GMT ~ Spark Therapeutics Inc Earnings Call scheduled for 8:30 am ET today
read full: http://biz.yahoo.com/cc/1/150021.html
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Wed, 06 May 2015 12:07:13 GMT ~ SPARK THERAPEUTICS, INC. Files SEC form 8-K, Results of Operations and Financial Condition, Financial Statements and
read full: http://biz.yahoo.com/e/150506/once8-k.html
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Wed, 06 May 2015 12:00:00 GMT ~ Spark Therapeutics Reports First Quarter 2015 Results
[GlobeNewswire] - PHILADELPHIA -- Spark Therapeutics today announced financial results for the quarter ended March 31, 2015.
read full: http://finance.yahoo.com/news/spark-therapeutics-reports-first-quarter-120000114.html
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$ONCE charts
basic chart ## source: stockcharts.com
basic chart ## source: stockscores.com
big daily chart ## source: stockcharts.com
big weekly chart ## source: stockcharts.com
$ONCE company information
## source: otcmarkets.com
Link: http://www.otcmarkets.com/stock/ONCE/company-info
Ticker: $ONCE
OTC Market Place: Not Available
CIK code: not found
Company name: Spark Therapeutics, Inc.
Incorporated In:
$ONCE share structure
## source: otcmarkets.com
Market Value: Not Available
Shares Outstanding: Not Available
Float: Not Available
Authorized Shares: Not Available
Par Value: Not Available
$ONCE extra dd links
Company name: Spark Therapeutics, Inc.
## STOCK DETAILS ##
After Hours Quote (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/after-hours
Option Chain (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/option-chain
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## COMPANY NEWS ##
Market Stream (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/stream
Latest news (otcmarkets.com): http://www.otcmarkets.com/stock/ONCE/news - http://finance.yahoo.com/q/h?s=ONCE+Headlines
## STOCK ANALYSIS ##
Analyst Research (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/analyst-research
Guru Analysis (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/guru-analysis
Stock Report (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/stock-report
Competitors (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/competitors
Stock Consultant (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/stock-consultant
Stock Comparison (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/stock-comparison
Investopedia (investopedia.com): http://www.investopedia.com/markets/stocks/ONCE/?wa=0
Research Reports (otcmarkets.com): http://www.otcmarkets.com/stock/ONCE/research
Basic Tech. Analysis (yahoo.com): http://finance.yahoo.com/q/ta?s=ONCE+Basic+Tech.+Analysis
Barchart (barchart.com): http://www.barchart.com/quotes/stocks/ONCE
DTCC (dtcc.com): http://search2.dtcc.com/?q=Spark+Therapeutics%2C+Inc.&x=10&y=8&sp_p=all&sp_f=ISO-8859-1
Spoke company information (spoke.com): http://www.spoke.com/search?utf8=%E2%9C%93&q=Spark+Therapeutics%2C+Inc.
Corporation WIKI (corporationwiki.com): http://www.corporationwiki.com/search/results?term=Spark+Therapeutics%2C+Inc.&x=0&y=0
## FUNDAMENTALS ##
Call Transcripts (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/call-transcripts
Annual Report (companyspotlight.com): http://www.companyspotlight.com/library/companies/keyword/ONCE
Income Statement (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/financials?query=income-statement
Revenue/EPS (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/revenue-eps
SEC Filings (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/sec-filings
Latest filings (otcmarkets.com): http://www.otcmarkets.com/stock/ONCE/filings
Latest financials (otcmarkets.com): http://www.otcmarkets.com/stock/ONCE/financials
Short Interest (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/short-interest
Dividend History (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/dividend-history
RegSho (regsho.com): http://www.regsho.com/tools/symbol_stats.php?sym=ONCE&search=search
OTC Short Report (otcshortreport.com): http://otcshortreport.com/index.php?index=ONCE
Short Sales (otcmarkets.com): http://www.otcmarkets.com/stock/ONCE/short-sales
Key Statistics (yahoo.com): http://finance.yahoo.com/q/ks?s=ONCE+Key+Statistics
Insider Roster (yahoo.com): http://finance.yahoo.com/q/ir?s=ONCE+Insider+Roster
Income Statement (yahoo.com): http://finance.yahoo.com/q/is?s=ONCE
Balance Sheet (yahoo.com): http://finance.yahoo.com/q/bs?s=ONCE
Cash Flow (yahoo.com): http://finance.yahoo.com/q/cf?s=ONCE+Cash+Flow&annual
## HOLDINGS ##
Major holdings (cnbc.com): http://data.cnbc.com/quotes/ONCE/tab/8.1
Insider transactions (yahoo.com): http://finance.yahoo.com/q/it?s=ONCE+Insider+Transactions
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Insider transactions (insidercrow.com): http://www.insidercow.com/history/company.jsp?company=ONCE
Ownership Summary (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/ownership-summary
Institutional Holdings (nasdaq.com): http://www.nasdaq.com/symbol/ONCE/institutional-holdings
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Insider Disclosure (otcmarkets.com): http://www.otcmarkets.com/stock/ONCE/insider-transactions
## SOCIAL MEDIA AND OTHER VARIOUS SOURCES ##
PST (pennystocktweets.com): http://www.pennystocktweets.com/stocks/profile/ONCE
Market Watch (marketwatch.com): http://www.marketwatch.com/investing/stock/ONCE
Bloomberg (bloomberg.com): http://www.bloomberg.com/quote/ONCE:US
Morningstar (morningstar.com): http://quotes.morningstar.com/stock/s?t=ONCE
Bussinessweek (businessweek.com): http://investing.businessweek.com/research/stocks/snapshot/snapshot_article.asp?ticker=ONCE
$ONCE DD Notes ~ http://www.ddnotesmaker.com/ONCE